In this FSH Society webinar, Scott Q. Harper, PhD, of Nationwide Children’s Research Institute describes FSHD genetics and explains how gene and molecular therapy could be used to block the genetic mechanism that is thought to cause muscle degeneration in facioscapulohumeral muscular dystrophy. The talk is very understandable to non-scientists and conveys the real sense of optimism that is transforming the field today.
Posted on: Dec 18, 2017
Ten years! Amazing progress by amazing minds, but I kmow how long it took leading up to that. Thank you for not giving up — for giving us hope and courage to fight on.