This invaluable data is coming to the FSHD Society by Lucienne Ronco, PhD, FSHD Society When a clinical trial fails, what happens to the data? It may include hundreds of… Read More »
The fate of the Fulcrum Phase 3 data
European Neuromuscular Centre Conference on Pediatric FSHD
by Ally Roets, Tucson, Arizona I was honored to attend the Pediatric FSHD European Neuromuscular Centre (ENMC) conference in Amsterdam, Netherlands, this past October. I was invited as a parent… Read More »
Big pharmas show growing interest in FSHD
By June Kinoshita, FSHD Society The pharmaceutical industry is showing a growing interest in developing therapies for facioscapulohumeral muscular dystrophy (FSHD), a rare genetic disorder affecting an estimated one million… Read More »
A personal mission to advance research
Amanda Hill, a Colorado native, lives with her husband, Justin, and their two dogs in the Denver area. Together, they share a love for travel, great food, and discovering new… Read More »
Science with a heart
Lucienne Ronco’s journey is a testament to the power of curiosity and compassion. With roots in the Pocono Mountains of Pennsylvania, she embarked on a path that would lead her… Read More »