By Angela Lek, PhD Yale University The discovery of CRISPR-Cas9 gene-editing technology has undoubtedly revolutionized the field of human genetics, enabling for the first time in human… Read More »
A new, improved CRISPR-Cas9 technology
miRecule, Inc., is developing a novel treatment for FSHD
In their offices in Maryland, just northwest of Washington, DC, miRecule Inc. and its founder Anthony Saleh, PhD, are hard at work developing a novel treatment for FSHD. In the… Read More »
Progress Report on Therapeutic Accelerator for FSHD
Last week, Mark Stone, the FSHD Society president and CEO, gave his fourth-quarter progress report on the Therapeutic Accelerator for FSHD treatments. His presentation was given via webinar to leadership… Read More »
The Fierce Urgency of Now
“We are now faced with the fact that tomorrow is today. We are confronted with the fierce urgency of now.” Thus Dr. Martin Luther King Jr. exhorted the nation at… Read More »
HAT Trick to Block the DUX4 Gene
Researchers Identify a New Compound that Inhibits the Activity of DUX4 By Alec DeSimone, PhD University of Massachusetts Medical School Led by a team at the University of Minnesota, Minneapolis,… Read More »