Patients who volunteer for research are the keystone of drug development efforts. Without them, the entire edifice built by teams of biologists, chemists, doctors, and other PhDs and MDs, would… Read More »
“Building the house” for FSHD therapies
Follistatin gene therapy strengthens muscle in FSHD mouse model
An experimental gene therapy has been shown to enlarge and strengthen muscles in a mouse model of facioscapulohumeral muscular dystrophy (FSHD). The study was published on November 15 in the… Read More »
Webinar with Stephen Tapscott MD PhD (video)
From our webinar on November 7, 2018. Dr. Tapscott, one of the world’s leading scientists working on the fundamental understanding of FSH muscular dystrophy, updates us on our understanding of… Read More »
High-intensity exercise training in FSHD
by Amanda Hill If you or a loved one is affected by FSHD, or any muscular dystrophy for that matter, chances are that you’ve heard it’s best not to exercise,… Read More »
DUX4 vs. PAX7–Who’s the fairest one of all?
by Amanda Hill For several years, DUX4 has enjoyed center stage in the yet-unfolding story of facioscapulohumeral muscular dystrophy (FSHD). DUX4 was first identified in 19991, but only in the… Read More »