[…] approach to treating facioscapulohumeral muscular dystrophy. She describes the company’s scientific research to develop “ FSHD in a dish” models to screen and identify candidate drugs that can suppress the […]
Fulcrum’s approach to treating FSH muscular dystrophy [VIDEO]
Voice of the Patient Forum [VIDEO]
[…] Voice of the Patient Forum (or patient-focused drug development meeting) for facioscapulohumeral muscular dystrophy ( FSHD) that is being organized by the FSHD Society for April 21. James Valentine explains […]
Losmapimod receives orphan drug designation
[…] Administration. Losmapimod is currently in a Phase 2 clinical trial for facioscapulohumeral muscular dystrophy ( FSHD). The drug qualified for this status because FSHD, with an estimated 20-40,000 affected individuals […]
What would be meaningful benefits of future treatments?
[…] safe. Join us on Thursday, March 26, at 1:00 PM ET, for our next live FSHD Society Sequester Camp webinar on “Ways to Connect. Ways to Help.” Please know that […]
‘Eddie-mechanics’ was my secret to success
[…] retirement months earlier as the exhaustion, discomfort, and worsening deterioration of my muscles caused by FSHD as well as my related digestive issues had simply become too great. The ACLU […]