[…] of this approach in a large animal model of Duchenne. What is the significance for FSHD? It has been shown previously that the CRISPR method can fix the DMD defect […]
Gene editing takes big step forward in Duchenne dog model
Don’t let this diagnosis limit you
[…] reaches at least one person and helps him or her understand that a diagnosis of FSHD or any other neuromuscular disease can be transcended. Growing up, I knew something was […]
Fulcrum Therapeutics raises $80 million in series B
[…] after filing papers with the FDA to begin human testing of its first drug, for FSHD, according the Fulcrum’s CEO, Robert Gould. “We think that the strength of the preclinical […]
Inaugural Walk & Roll Campaign a Tremendous Success!
[…] REYNOLDS, Kansas City, Missouri When we began planning for the inaugural Walk & Rolls to Cure FSHD, a $105,000 fundraising goal felt ambitious. Then an incredible group of volunteer leaders stepped […]
Holiday gift ideas
[…] hear about your best holiday gift ideas in the comments section! Reusable drinking straws. While FSHD can make it hard for some to sip through a straw, many others rely […]